Aron Jaffe
@jaffeab
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SVP @ https://t.co/5bCQBx9DVy;Former SVP Head of Research @chromamedicine;EIR @ThirdRockV;Reg Med, uBiome group leader/Resp DA co-lead @NovartisScience. Opinions mine
Boston, MA
Joined October 2011
Our work describing the development of a potent epigenetic editor targeting human #PCSK9 for durable reduction of LDL-C is out in @NatureMedicine today!.Cc: @chromamedicine @nchromabio.1/9.
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How we’re rebuilding the Weizmann Institute — and our hopes for a better future
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Happy Father’s Day to @rcjaffe & all the Dads out there!. I dont @ him often, but 👇🏼 is one of my favorites.
My father @rcjaffe officially retired this week. His last day @UICPhysiology was Monday, 8/31. Although my Dad always described himself as ‘small potatoes’, and since there was no departmental send-off, I wanted to highlight a few things about his career (thread).
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RT @Carolynyjohnson: In case you needed a smile this Tuesday: 10-month-old baby KJ, who received a bespoke gene-editing therapy after a six….
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When a therapeutic approach works, it's on us as a global community to figure out how to get it to ALL patients in need. Great piece by @Jasonmmast . What Baby KJ means for the CRISPR gene editing industry via @statnews.
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Absolutely amazing. Congratulations to @kiranmusunuru @UrnovFyodor & everyone involved.
Today "a milestone in the evolution of personalized therapies for rare & ultra-rare inborn errors of metabolism".—the 1st human to undergo custom genome editing.—outgrowth of decades of NIH funded research.@NEJM
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FDA delays are bad in general, but for a small biotech they can be existential. Let’s hope this is an edge case.
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“The most effective way to prevent the spread of measles is the MMR vaccine”.
I came to Gaines County, Texas, today to comfort the Hildebrand family after the loss of their 8-year-old daughter Daisy. I got to know the family of 6-year-old Kayley Fehr after she passed away in February. I also developed bonds with and deep affection for other members of.
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Congratulations @davidrliu!.
David Liu receives Breakthrough Prize in Life Sciences. @davidrliu is honored for the development of base editing and prime editing, two gene editing technologies transforming medicine. @brkthroughprize
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RT @doctorveera: I and my colleague, Sahar Gelfman, at RGC had the privilege to write a News and Views article for @nature about a recent w….
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If anything cool actually came from this effort, this would be one of the sickest hockey photos ever
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This is a big day for patients with AATD and a big win for genomic medicine. Congrats to the entire Beam Team @BeamTx!.
Today, Beam announced positive initial data for BEAM-302 from its Phase 1/2 trial in alpha-1 antitrypsin deficiency (AATD), establishing clinical proof-of-concept and demonstrating the first ever clinical gene editing correction of a disease-causing mutation.
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Congratulations to @bigosi @SethEttenberg & the entire @BlueRockTx team! . BlueRock Therapeutics receives FDA Fast Track Designation for OpCT-001 for the treatment of primary photoreceptor diseases
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