With the aim of getting a cross-section of the current state of progress in #celltherapy for #solidtumors, CGTLive® reached out to several experts to get their insight into some notable approaches under evaluation. #oncology #CART #solidtumor. More:.

ICYMI:. RP-A701 utilizes an AAVrh.74 vector and constitutes a first-in-class treatment for BAG3-DCM. #genetherapy #CardiologyTwitter #cardiomyopathy @RocketPharma. Read more:.

ICYMI:. With the removal of the REMS requirement, hospitals and clinics that provide these therapies no longer necessitate a specific certification. #CART #celltherapy #FDA @US_FDA. Read more:.

"This is encouraging for us because it does potentially pave the path for us exploring the ability to redose our therapy. " -Derek Jackson, BS, MA (@PaciraBio). #osteoarthritis #genetherapy #KneeOsteoarthritis #ASGCT2025 . Watch:.

The 24 patients in group 1 who received rilparencel showed stabilization of kidney function following treatment, with a 78% improvement in annual decline in eGFR slope. #diabetes #KidneyDisease #CKD #celltherapy @ProKidney. Read more:.

SNUG01 has previously been evaluated in an investigator-initiated trial in China that was completed recently, according to @Sineugene_2021. #ALS #genetherapy #AmyotrophicLateralSclerosis. Read more:.

Notably, @CARsgen_Ther received priority review for satri-cel from the NMPA in May 2025 for the indication covered in the NDA. #GastricCancer #CART #celltherapy. Read more:.

With the removal of the REMS requirement, hospitals and clinics that provide these therapies no longer necessitate a specific certification. #CART #celltherapy #FDA @US_FDA. Read more:.

This Fourth of July, we honor the relentless pursuit of progress that transforms patient care and shapes the future of medicine. Wishing everyone a safe and inspiring holiday. #FourthofJuly #IndependenceDay

ICYMI:. Our team has highlighted several important actions including the @US_FDA granting its new platform designation to @Sarepta and clearing an IND application for #Nuevocor's LMNA DCM #genetherapy. #celltherapy. More:.

ICYMI:. "I personally have seen very positive outcomes as far as efficacy in all that I've treated so I think that's very exciting." -Tami John, MD (@StanfordMed). #thalassemia #genetherapy #hematology. More:.

RP-A701 utilizes an AAVrh.74 vector and constitutes a first-in-class treatment for BAG3-DCM. #genetherapy #CardiologyTwitter #cardiomyopathy @RocketPharma. Read more:.

Patients with DLBCL who were treated with tisa-cel, axi-cel, or liso-cel across their FDA-approved indications did not show statistically significant differences in overall survival. #lymsm #lymphoma #EHA2025. Read more:.

Last month delivered data updates from several conferences, including #ASCO25, #ADASciSessions, and #EHA2025. Click here:.

ICYMI:. ". so far, for both products, we haven't seen numbers that indicate one is more difficult or problematic than the other." -Tami John, MD (@StanfordMed). #thalassemia #genetherapy #hematology. Watch now:.

Our team has highlighted several important actions including the @US_FDA granting its new platform designation to @Sarepta and clearing an IND application for #Nuevocor's LMNA DCM #genetherapy. #celltherapy. More:.

ICYMI:. According to enGene, data from the phase 1/2 LEGEND study informed the FDA’s decision to grant RMAT designation to detalimogene. #genetherapy #BladderCancer #oncology. Read more:.

"I personally have seen very positive outcomes as far as efficacy in all that I've treated so I think that's very exciting." -Tami John, MD (@StanfordMed). #thalassemia #genetherapy #hematology. More:.

ICYMI:. The study is open to patients aged 18 years and older who have clinically diagnosed #SolidTumors of various types and require antitumor therapy on a routine basis. #oncology #celltherapy #solidtumor #ClinicalTrialsInProgress. Read more:.

ICYMI:. Both deaths occurred in patients who were nonambulatory at the time of treatment and who had been hospitalized within 2 months of treatment in relation to raised levels of transaminases. #Duchenne #MuscularDystrophy #genetherapy @Sarepta . More:.