Today we celebrate the spirit of freedom, resilience, & possibility that helps us continue our mission to bring life-changing gene therapies to patients with #RareDiseases. Wishing everyone a happy and meaningful #IndependenceDay!

#TeamRocket was proud to sponsor & attend the Annual San Diego Heart Failure Summer Symposium this past month! Check out these great photos of our team connecting w/ leading minds in #cardiovasculardisease & exploring advancements in the field. @SD_HeartFailure

#TeamRocket is proud to sponsor the 31st Annual San Diego Heart Failure Symposium from 6/27 – 6/28! We’re looking forward to connecting w/experts on the latest advances in #heartfailure, #genetherapy & more. ➡️: .@SD_HeartFailure

Happy #PrideMonth! Rocket Pharmaceuticals is proud to support and recognize the LGBTQIA+ community within #TeamRocket & beyond. Our Social Committee encouraged us to Show Our Pride w/a cupcake decorating event 🏳️‍🌈

Thanks to all who joined our webinar with @GeneticCouns on the power of #GeneticTesting and counseling for those impacted by inherited, #RareDiseases like #DanonDisease. Watch the replay:

#News from #ASGCT2025: #TeamRocket presents preliminary data for the first time from the Phase 1 study of RP-A601, an investigational #GeneTherapy for the treatment of plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM). Learn more:

#TeamRocket is looking forward to the @ASGCTherapy annual meeting next week! We will present preliminary Phase 1 data for plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM) in a late-breaking oral presentation. Learn more: #ASGCT2025

This #FanconiAnemia Awareness Month, #FCF2025, #TeamRocket stands with patients and caregivers impacted by Fanconi anemia and remains committed to understanding their experience and advancing investigational new medicines. See below for more and in full:

This #NationalDNADay we celebrate the impact of genomics on modern medicine. #TeamRocket is on a mission to seek gene therapy cures for patients with devastating #RareDiseases through the most innovative science and platforms. #DNADay #Genetics #Genomics

#WorldPIWeek 2025 is here! #TeamRocket is committed to raising awareness about Primary Immunodeficiencies (PI) and supporting the global PI community. We're advancing #GeneTherapy to offer hope for those impacted by #RareDiseases like LAD-I. Learn more:

At #WorldOrphanUSA, #TeamRocket President, Head of R&D, and COO Kinnari Patel, PharmD, MBA, joins the keynote panel on the future of #RareDisease R&D to bring innovative therapies to people with rare diseases. More:

On April 22, #TeamRocket will host a webinar with.@GeneticCouns on the potential of #GeneTherapy to provide a one-time treatment for inherited cardiomyopathies, including #Danon disease, featuring Jonathan Schwartz, Chief Medical & Gene Therapy Officer.

Next week, #TeamRocket President, Head of R&D, and COO Kinnari Patel, PharmD, MBA will join a panel at the @alliancerm Cell & Gene Meeting on the Med. Learn more:

#TeamRocket is sharing poster presentations at two upcoming medical meetings: #AMCP2025 and #ISHLT2025. We look forward to connecting with fellow attendees and sharing our mission to fulfill the promise of #GeneTherapy for patients with devastating #RareDiseases. @AMCPorg @ISHLT

We’re heading to #ACC25 this week! We’re looking forward to joining the latest industry research, drug development, and patient discussions as we progress three AAV #GeneTherapy programs that could impact +100k patients in the U.S. and EU. More:

From our live event, to ringing the @Nasdaq bell, to lighting up @EmpireStateBldg, and much more, this #RareDiseaseDay was one to remember. Thank you for supporting our mission!. Watch the replay: @DanonFoundation @RareDiseaseDay @CharitableRTW @wishnj

We’re onsite at the @rarediseasesnet Primary Immune Deficiency Treatment Consortium. As bronze level sponsors, we’re joining others working to improve outcomes for patients with rare, life-threatening, inherited disorders of the immune system.

Seeing major buildings lit up in support of #LightUpForRare for #RareDiseaseDay was incredibly inspiring. Thank you to all who participated— together, we’re spreading awareness and sparking change. Let’s continue lighting the way for #RareDisease advocacy and progress!

RT @NYSE: The NYSE lights the façade to raise awareness for #RareDiseaseDay in collaboration with @RocketPharma!

We’re thrilled to have rung the opening bell at @Nasdaq on #RareDiseaseDay!. We’re overwhelmed with gratitude at the opportunity to commemorate this important day & show our dedication, commitment, & mission to seek gene therapy cures for patients with devastating rare diseases.