The 13th London Myology Forum is taking place on the Wednesday 4th June 2025 at the Elvin Hall, UCL IOE, 20 Bedford Way, WC1H 0AL. Free event, registration required by contacting Jane at jane.miller@ucl.ac.uk

5 Partners & 1 Associated partner of #EFFecT are present at SMOT (Synergistic Meeting on Oligonucleotide Therapeutics) celebrating #rarediseaseday. We are looking forward to start working together! Remember we are recruiting until March 15!!!📢 https://t.co/WW8XBemxqP

I'm excited to share that I have started a new role as a Research Fellow at @UCLchildhealth where I'll be working in Prof. @lab_zhou research group developing cell-targeting peptides for nucleic acid delivery.

We are delighted to announce today the inaugural 2024 Oxford-Harrington Rare Disease Scholars, selected from a large number of outstanding proposals from the US, UK and Canada, to develop breakthrough treatments for #rarediseases. Congratulations to the ten Scholars!

Oxford-Harrington is delighted to welcome Lord Cameron @David_Cameron as Chair of our Advisory Council, leading our international efforts to drive the Centre’s mission of delivering 40 new therapies for rare diseases into clinical trials over the coming decade.

Huge congratulations to Pambos, Konstantina @konstantina_tet and Ivan, our young talents who have won the best presentation Prizes from the World Muscle Society International Congress in Prague! Very proud of you 👏🎉 @DNP_ICH @GGM_ICH

📢 Calling all UK neuromuscular researchers and friends of @MDUK_News at #WMS2024 – pop along to stand 32 and chat to John about all things research and our grant round https://t.co/8Meszpe9y8 👥🗣️👩‍🦼💡🧬🔬💊🩺🧪

An exciting Research Assistant position in the Zhou Lab on RNA drug development. here is the applicaiton link: https://t.co/ToERAl07Rt Application deadline 20th Oct 2024. Please do help circulate it.

Exciting to hear about how UPNAT will support and drive development of nucleic acid therapeutics across the UK under Prof Zhou's leadership! #OxfordHarrington2024 @RDRUKHub @UCLchildhealth @lab_zhou

We shared the excitement as Haiyan Zhou @lab_zhou presented an update on her research as Harrington Scholar @HarringtonDI_UH. And appreciated the introduction to our @UpNAT_node! #OxfordHarrington2024 @OHRareDisease @RDRUKHub #RareDisease

Really inspiring and thought provoking discussions around the patient, disease and variant selection process for rare disease RNA therapy development @UpNAT_node

Today we are in London at the Inaugural Symposium of the UK Platform for Nucleic Acid Therapies @UpNAT_node @RDRUKHub which set to be an invaluable resource for the #raredisease community. Introduction by @lab_zhou the Director of UPNAT

Registration for tomorrow's Symposium has closed https://t.co/W32Htmo9IW For late registration, contact UPNAT@ucl.ac.uk. Thanks to the UPNAT Team for putting together what promises to be an exciting event! @lab_zhou @aliceedavidson @MinaRyten @njlench @rinaldi_ca @RDRUKHub

🔦Speaker Spotlight🔦 David Fischer, Chief Technology Officer for Discovery at Charles River Labs @CRiverLabs, will provide industry perspective at the upcoming @UpNAT_node Symposium. Register for our event, this Thursday 27 June at UCL ICH➡️ https://t.co/W32Htmo9IW

🔦 Speaker Spotlight 🔦 Ana Lisa Taylor Tavares, Clinical Lead for #RareDisease #Research at @GenomicsEngland, will look at collaborations across the UK Rare Disease research landscape. Spaces available for #UPNAT Symposium on 27 June ➡️register here ➡️ https://t.co/W32Htmo9IW

🔦 Speaker Spotlight 🔦 Stephan Sanders, Prof of Neurogenetics @OxPaediatrics, will speak next week at the #UPNAT Symposium about academic efforts in target selection for #raredisease Registration for 27 June @UCLchildhealth ➡️ https://t.co/W32HtmnBTo @UniofOxford @OxfordMedSci

Agenda confirmed for the UPNAT Symposium, with focus on 1) NAT Target Selection for Rare Disease, and 2) Clinical trials and Regulatory Path. Registration is open https://t.co/DjZLBGXTT6 27 June at @UCLchildhealth #RareDisease #NucleicAcid #ClinicalTrials

The UPNAT Node is grateful to the Oligonucleotide Therapeutics Society for their support of our upcoming Symposium on 27 June 2024 in London (registration now open: https://t.co/DjZLBGXm3y) More info about @OTSociety Delivery Grants here: https://t.co/g8vgOTTmUu

Interested in RNA therapies for rare disease? sign up for our upcoming @UpNAT_node symposium

An impressive line-up of speakers confirmed for the upcoming UPNAT Symposium! Full details below. Registration is open, 27 June in person at UCL Institute of Child Health https://t.co/32cyGEhUf6