Philippa Ward discusses her journey as the mother of a child diagnosed with tuberous sclerosis complex, the challenges posed by the condition’s complexities, and how she found both a community and her own voice as an advocate. @GlobalGenes #RARECast https://t.co/yRVx3UcGBC

Aaron Cohen, Head of Research Oncology, Clinical Data at @flatironhealth , joins Amar Drawid, on Life Sciences DNA to explore how large language models are transforming oncology research. https://t.co/VCPrEFUvgx

Stacy Lindborg, CEO of Imunon, discusses the company’s DNA-mediated immunotherapy, how it avoids the systemic toxicities that undermined earlier IL-12 approaches, and how it could change the treatment landscape for the disease. https://t.co/YN9JYcUypl

The Rwanda FDA approved @BioUsawa 's BioUcenta, a biosimilar of Lucentis. It is the first biosimilar ranibizumab approved in Africa and represents the first major regulatory milestone for Bio Usawa. https://t.co/jyWoFGpBtt

Laura Russo, U.S. patient engagement lead for @pfizer , discusses how the company’s patient-facing teams work to bridge health systems and patient communities to improve access and care. @GlobalGenes #RARECast https://t.co/J7FcMClHOM

.@DrewEndy @HooverInst @Stanford discusses China’s all-of-nation strategy, how the US has misallocated research dollars, and why a cultural embrace of biotechnology will be critical for the success of either country. https://t.co/FQMd8xkRpo

Kristin McKay @Projectalive discusses the need for new therapies for Hunter syndrome, the importance of early detection, and the patient community’s concerns with regulatory delays in approving needed treatments. @GlobalGenes #RARECast https://t.co/U335o0rFNt

Amélie Lothe, global medical community head for rare epilepsies at @UCBUSA, discusses the need to look beyond seizures to view developmental and epileptic encephalopathies as complex neurodevelopmental conditions. @GlobalGenes #RARECast https://t.co/xLbBL1nQMB

Marc Salzberg @Airway_Tx discusses the company’s experimental therapy zelpultide alfa to treat preterm infants with a rare lung disease, why it’s a pipeline-in-a-product, and its development path forward. https://t.co/8Xprjap671

Here's what you may have missed in September from The Bio Report, RARECast, and Life Sciences D'n'A podcasts. https://t.co/dktZPttsrx

Todd Harris @TyraBiosciences discusses the company’s experimental oral medicine for achondroplasia, studies conducted to date, and why he believes it will offer competitive advantages over existing therapies. @GlobalGenes #RARECast https://t.co/FcLE7JfiWD

What happens when AI touches every role, every day, in clinical development? Stephen Pyke of @Parexel, in conversation with Nagaraja Srivatsan, highlights why preparing teams early is essential to unlock their full potential. trials? https://t.co/O641o9XFmK

Rohan Palekar, CEO of 89bio, discusses what’s driving the prevalence of MASH, the limits of existing medicines, and how the company’s experimental therapy targets both liver fibrosis and the underlying metabolic dysfunctions of the disease. https://t.co/m180Ii8Y18

.@paulpetertak @CandelTx discusses the company's viral immunotherapy for brain cancer, how it works, and what clinical studies have shown to date. @GlobalGenes #RARECast https://t.co/DsMOSFXLZf

Steve Perrin, CSO of @Eledon_Pharma, discusses the need for innovative approaches to immunosuppression in organ transplantation, how its experimental therapy works, and why it may have benefits in autoimmune and neurodegenerative diseases as well. https://t.co/7zJkMSOJ2v

David Jenkinson @lifearc1 discusses the children’s cancer therapeutics consortium C-Further, the challenges of developing treatments for childhood cancers, and why new models for advancing these therapies are needed. @GlobalGenes #RARECast https://t.co/kvxpg5JS8B

Mohan Uttarwar, CEO of @1cellAi , discusses how AI-powered cell biopsy could make cancer monitoring more accessible, minimally invasive, and transformative for millions of patients worldwide https://t.co/b8i902GoJT

Greg Mario, CEO of Taxis Pharmaceuticals, discusses the public health threat posed by drug-resistant gonorrhea, the approaches it’s taking to develop new antimicrobial treatments, and the need for new funding models to bring new therapies to market. https://t.co/FMNFIhU1d8

Robin Williams of @umnmedschool @UMNews Masonic Children's Hospital discusses the medical mystery of a 15-year-old admitted into a PICU and what it took to diagnose him with the ultra-rare disease TAFRO. @globalgenes #RARECast https://t.co/ZdBHyWbZVP

Marc Hedrick, CEO of @plustxinc, discusses the challenges of treating brain tumors, the limitations of current therapies, and why the company’s targeted radiotherapies have the potential to create better outcomes for patients. https://t.co/vIjjzeC30r