cf/Aware
@CFAware
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All about Cystic Fibrosis. Always refer to your team for specialist advice. Oh and we don't always agree with RTs.
Joined February 2012
Kalydeco = ivacaftor Orkambi = lumacaftor + ivacaftor Symkevi = tezacaftor + ivacaftor Kaftrio = elexacaftor+tezacaftor+ ivacaftor
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Excited to offer participation in GRAMPUS-CF to patients with cystic fibrosis worldwide. Just click on the link to join the study! https://t.co/EnAha4Gjfo
@cftrust @CF_Foundation @alloonsl @CFAware
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$VRTX on pace to lose $15B in market value today.
$VRTX - That was a bad quarter. Every product missed. Lower end of guidance raised -- who cares? Lots of handwaving around Journavx access but insignificant revenue. Casgevy is a money loser. The stock is near an all-time high and trades at 26x, Vertex needs to do better. The
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Today the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for our fifth cystic fibrosis (CF) medicine. This is an important step towards our goal of treating all people living with CF.
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Today the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for the label expansion of our fourth cystic fibrosis (CF) medicine to include an expanded population with certain mutations. This marks an important step
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Mycobacterium Abscessus Infections and Cystic Fibrosis | Nature Research Intelligence
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Cystic Fibrosis and Fungal Infections | Nature Research Intelligence
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Do intravenous antibiotics improve pulmonary exacerbations (flare-ups) in people with cystic fibrosis? | Cochrane
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Body composition changes and clinical outcomes in pediatric cystic fibrosis during 24 months of lumacaftor ivacaftor therapy based on real-world data | Scientific Reports
nature.com
Scientific Reports - Body composition changes and clinical outcomes in pediatric cystic fibrosis during 24 months of lumacaftor ivacaftor therapy based on real-world data
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🚨 New in The Lancet Respiratory Medicine Phase 3 data on vanzacaftor–tezacaftor–deutivacaftor in #cysticfibrosis Read open access here: Patients aged 6–11 years https://t.co/d7R7w1hsgo Patients aged 12 years and older https://t.co/Xl4qJtcS2C
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GRAMPUS-CF aims to understand gut symptoms in people with cystic fibrosis (CF) so that we can develop treatments. If you are a person with CF, you can help! Visit our website for participant information, online consent and to download the app. https://t.co/FoOUpNDK8x Thank you!
grampus-cf.org
Join the GRAMPUS-CF study to explore gut symptoms in cystic fibrosis and help develop personalized treatments. Enroll online or via CF centers.
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NICE Board says new method allowing greater weight to be given to severe diseases is working | NICE
nice.org.uk
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Boy, 3, has combination of CFTR mutations, no CF symptoms: Report
cysticfibrosisnewstoday.com
The boy's case underscores the challenges of predicting outcomes in CF, especially when rarer mutations are involved, the researchers said.
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NICE approves three cystic fibrosis drugs for NHS use - The Pharmaceutical Journal
pharmaceutical-journal.com
Three cystic fibrosis (CF) drugs have been approved for use on the NHS by the National Institute for Health and Care Excellence (NICE), after not initially recommending them in draft guidance. In...
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UK #CysticFibrosis community! Tell us about your thoughts on inhaled meds & interacting with your care providers post-Kaftrio in this anonymous 5-10 min research survey. Your voice matters! Please share! [ https://t.co/HDX6Qjf1CY]
#CF
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Trikafta revolutionized treatment for Cystic Fibrosis, reaching >90% of patients variants. But what about the remaining untreatable 10%? We studied several poorly responsive, FDA-unapproved variants and paved a path forward for drug development. https://t.co/cGQOqYegwe 1/7
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CF patients eat high-fat diet despite guidelines: Review
cysticfibrosisnewstoday.com
Many adults with CF eat high-fat, high-energy diets despite guidelines recommending otherwise, a review study found.
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